Zegen Our science Gene Therapy | Zegen Therapeutics

Gene therapy is the process of modifying a patient’s cells by adding a functional copy of the mutated gene which is causing the patient disease. The new functional copy allows a patient’s own body to produce proteins to treat or prevent genetic conditions. A single treatment can provide long lasting benefits, potentially leading to a better quality of life. Our research and clinical expert’s gene therapy experience allows us at ZeGen to design and construct all critical gene therapy elements and bring them together to develop successful treatments for patients.

Zegen Our science Gene Therapy | Zegen Therapeutics

Gene therapy is the process of modifying a patient’s cells by adding a functional copy of the mutated gene which is causing the patient disease. The new functional copy allows a patient’s own body to produce proteins to treat or prevent genetic conditions. A single treatment can provide long lasting benefits, potentially leading to a better quality of life. Our research and clinical expert’s gene therapy experience allows us at ZeGen to design and construct all critical gene therapy elements and bring them together to develop successful treatments for patients.

Key Features of ZeAAV5 Gene Therapy

  • COMPACT CAPSID DESIGN

  • NEURO-SPECIFIC TARGETED DELIVER
  • VARIABLE EXPRESSION GENE CASSETTESC
  • NEURO-SPECIFIC PROMOTERS
  • cGMP MANUFACTURING PARTNERS
  • NOVEL FORMULARY